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人类有超过75000种疾病与遗传变异相关,其中大部分是单碱基突变。因此,构建基因点突变细胞株,在疾病的检测、研究与治疗中,具有巨大的应用潜力。
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Generation of Human Isogenic Induced Pluripotent Stem Cell Lines with CRISPR Prime Editing
Structural basis for pegRNA-guided reverse transcription by a prime editor

A truncated reverse transcriptase enhances prime editing by split AAV vectors

Structural basis for pegRNA-guided reverse transcription by a prime editor





